National Institutes of Health (NIH)

Infant with rare, incurable disease is first to successfully receive personalized gene therapy treatment

NIH-supported gene-editing platform lays groundwork to rapidly develop treatments for other rare genetic diseases.

Poly-metabolite scores could reduce reliance on self-reported dietary data in large population studies.

NIH-funded breakthrough could enable targeted therapies for many neurological disorders.

The technique may enable higher doses and combinations of cell therapies.

RTX is a non-addictive pain therapy derived from a cactus-like plant.

NIH-funded project shows that trans-epidermal water loss could indicate if wounds are fully healed.